Awaiting development: Guidance and quality standards
Showing 1 to 2 of 2
Title | Type |
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Doxecitine–doxribtimine for treating thymidine kinase 2 deficiency in people of any age who had symptoms before 13 years ID6484 | Highly specialised technology |
OTL-101 for treating adenosine deaminase deficiency–severe combined immunodeficiency [ID1152] | Highly specialised technology |