Tafamidis for treating transthyretin amyloidosis with cardiomyopathy (TA984)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 19 June 2024
Mavacamten for treating symptomatic obstructive hypertrophic cardiomyopathy (TA913)Product type:GuidanceProgramme:Technology appraisal guidancePublished: 6 September 2023
Vutrisiran for treating transthyretin-related amyloidosis cardiomyopathy [ID6470]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 12 November 2025
Acoramidis for treating transthyretin-related amyloidosis cardiomyopathy ID6354Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Eplontersen for treating transthyretin-related amyloidosis cardiomyopathy [TSID12015]Status:Awaiting developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Mavacamten for treating symptomatic non-obstructive hypertrophic cardiomyopathy [ID6523]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Elamipretide for treating Barth syndrome in people of any age [ID6545]Status:Topic selectionProgramme:Technology appraisal guidanceExpected publication date: TBC