Somapacitan for treating growth hormone deficiency in people 3 to 17 years [ID6178]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 29 May 2025
Sodium zirconium cyclosilicate for treating hyperkalaemia (partial review of TA599) [ID6439]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 17 December 2025
Vutrisiran for treating transthyretin-related amyloidosis cardiomyopathy [ID6470]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: 28 January 2026
Burosumab for treating FGF23-related hypophosphataemia in tumour-induced osteomalacia [ID3924 ]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Leriglitazone for treating andrenoleukodystrophy [ID3903]Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Pegzilarginase for treating arginase-1 deficiency [ID4029]Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC
Venglustat for treating gangliosidoses in people 2 years and over ID 6358Status:In developmentProgramme:Technology appraisal guidanceExpected publication date: TBC
Doxecitine–doxribtimine for treating thymidine kinase 2 deficiency in people of any age ID6484Status:In developmentProgramme:Highly specialised technologies guidanceExpected publication date: TBC