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Guidance programme

Showing 1 to 15 of 20 results for amyloidosis

  1. Inotersen for treating hereditary transthyretin amyloidosis (HST9)

    Evidence-based recommendations on inotersen (Tegsedi) for stage 1 and stage 2 polyneuropathy in adults with hereditary transthyretin amyloidosis.

  2. Patisiran for treating hereditary transthyretin amyloidosis (HST10)

    Evidence-based recommendations on patisiran (Onpattro) for treating hereditary transthyretin amyloidosis in adults with stage 1 and stage 2 polyneuropathy.

  3. Eplontersen for treating hereditary transthyretin-related amyloidosis (TA1020)

    Evidence-based recommendations on eplontersen (Wainzua) for treating hereditary transthyretin-related amyloidosis in adults.

  4. Vutrisiran for treating hereditary transthyretin-related amyloidosis (TA868)

    Evidence-based recommendations on vutrisiran (Amvuttra) for treating hereditary transthyretin-related amyloidosis in adults.

  5. Vutrisiran for treating transthyretin-related amyloidosis cardiomyopathy [ID6470]

    In development [GID-TA11598] Expected publication date: 12 November 2025

  6. Daratumumab in combination for treating newly diagnosed systemic amyloid light-chain amyloidosis (TA959)

    Evidence-based recommendations on daratumumab (Darzalex) for newly diagnosed systemic amyloid light-chain amyloidosis in adults.

  7. Tafamidis for treating transthyretin amyloidosis with cardiomyopathy (TA984)

    Evidence-based recommendations on tafamidis (Vyndaqel) for treating transthyretin amyloidosis with cardiomyopathy in adults.

  8. Acoramidis for treating transthyretin-related amyloidosis cardiomyopathy ID6354

    In development [GID-TA11415] Expected publication date: TBC

  9. Sebetralstat for treating acute attacks of hereditary angioedema in people aged 12 and over [ID6284]

    In development [GID-TA11334] Expected publication date: 17 December 2025

  10. Eplontersen for treating transthyretin-related amyloidosis cardiomyopathy [TSID12015]

    Awaiting development [GID-TA11551] Expected publication date: TBC

  11. Technology appraisal and highly specialised technologies appeals

    Technology appraisal and Highly specialised technologies appeals

  12. CAEL-101 with standard care for untreated amyloid light chain amyloidosis [ID6210]

    Awaiting development [GID-TA11182] Expected publication date: TBC

  13. Taking a proportionate approach to technology appraisals

    Find out more about NICE's new proportionate approach to technology appraisals

  14. Pancreatitis (NG104)

    This guideline covers managing acute and chronic pancreatitis in children, young people and adults. It aims to improve quality of life by ensuring that people have the right treatment and follow-up, and get timely information and support after diagnosis.

  15. Myeloma: diagnosis and management (NG35)

    This guideline covers the diagnosing and managing of myeloma (including smouldering myeloma and primary plasma cell leukaemia) in people aged 16 and over. It aims to improve care for people with myeloma by promoting the most effective tests and treatments for myeloma and its complications.