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Pegzilarginase for treating arginase-1 deficiency in people 2 years and over

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2 Information about pegzilarginase

Marketing authorisation indication

2.1

Pegzilarginase (Loargys, Immedica) is indicated 'for the treatment of arginase‑1 deficiency (ARG1‑D), also known as hyperargininemia, in adults, adolescents and children aged 2 years and older'.

Price

2.3

The list price for pegzilarginase is £4,690.00 per 2‑mg vial (excluding VAT, company submission).

2.4

The company has a commercial arrangement (simple discount patient access scheme), which would have applied if pegzilarginase had been recommended. The size of the discount is commercial in confidence.