Cerliponase alfa for treating neuronal ceroid lipofuscinosis type 2

Final evaluation determination: 2

Final evaluation determination document (PDF 345 KB)

Committee papers (PDF 731 KB)

Public committee slides (PDF 848 KB)

Committee papers Managed Access Agreement (PDF 453 KB)

Appeal

Batten Disease Family Association : Appeal letter (PDF 360 KB)

Batten Disease Family Association : Scrutiny letter (PDF 410 KB)

Batten Disease Family Association : Response to scrutiny letter (PDF 169 KB)

Batten Disease Family Association : Final scrutiny letter (PDF 253 KB)

Final evaluation determination

Final evaluation determination document (PDF 390 KB)

Committee papers (PDF 7.16 MB)

Public committee slides (PDF 1.4 MB)

Evaluation consultation: 1

Evaluation consultation document (PDF 508 KB)

Committee papers (PDF 31.89 MB)

Public committee slides (PDF 420 KB)

Final scope (PDF 229 KB)

NICE's response to comments on the draft scope and provisional matrix (PDF 366 KB)

Final matrix (PDF 258 KB)

Equality impact assessment (Scoping) (MSWord 39 KB)

Draft scope pre referral (PDF 128 KB)

Draft matrix pre referral (PDF 98 KB)