2 Information about etranacogene dezaparvovec

Marketing authorisation indication

2.1

Etranacogene dezaparvovec (Hemgenix, CSL Behring) has a conditional marketing authorisation 'for the treatment of severe and moderately severe haemophilia B (congenital factor IX deficiency) in adult patients without a history of factor IX inhibitors'.

Dosage in the marketing authorisation

Price

2.3

The list price per treatment for a single dose of etranacogene dezaparvovec is £2,600,000.

2.4

The company has a commercial arrangement. This makes etranacogene dezaparvovec available to the NHS with a discount. The size of the discount is commercial in confidence.