Nusinersen for treating spinal muscular atrophy

Supporting evidence

• Evidence review

• Review outcome summary  (PDF 223 KB)

  Published:

  04 June 2021

• Company evidence submission (PDF 2.38 MB)

  Published:

  04 June 2021

• External Assessment Centre (EAC) report (PDF 466 KB)

  Published:

  04 June 2021

• Company responses to EAC report (PDF 905 KB)

  Published:

  04 June 2021

• Managed Access Oversight Committee (MAOC) recommendation report (PDF 162 KB)

  Published:

  04 June 2021

• NICE summary slides (PowerPoint 636 KB)

  Published:

  04 June 2021

• Outline of objectives  (PDF 209 KB)

  Published:

  04 June 2021

• Evidence review process (PDF 115 KB)

  Published:

  29 October 2020

• Nusinersen managed access agreement clinical eligibility criteria evidence review: timeline

• Evaluation report

• Final appraisal determination committee papers (PDF 5.4 MB)

  Published:

  24 July 2019

• Appraisal consultation committee papers (PDF 15.7 MB)

  Published:

  24 July 2019